Supporters
Supporters
Thank you to our supporters for making our
2024 meeting a great success
Platinum
Acadia Pharmaceuticals
Catalyst
Cook Children’s Global Health
GeneDx
Gold
Biomarin
Sage Publishing
Bronze
Ipsen
Jazz Pharmaceuticals
Mayo Labs
Marinus
Neurelis
NS Pharma
Novartis
PTC
Sanofi
Sarepta
UCB
Ultragenyx
Zeto