Supporters

Supporters

Thank you to our supporters for making our
2024 meeting a great success

Platinum

Acadia Pharmaceuticals
Catalyst
Cook Children’s Global Health
GeneDx

Gold

Biomarin
Sage Publishing

Bronze

Ipsen
Jazz Pharmaceuticals
Mayo Labs
Marinus
Neurelis
NS Pharma
Novartis
PTC
Sanofi
Sarepta
UCB
Ultragenyx
Zeto